From: Current advances in gene therapy of mitochondrial diseases
Organ | Serotype | References |
---|---|---|
Brain | AAV2 | [66], [67], [68] |
AAV5 | [69] | |
AAV8 | [70] | |
AAV9 | [58], [71], [72] | |
AAVrh.10 | [58], [73], [74], [75], [76] | |
Retina | AAV5, AAV2-HBKO | [77] |
AAV2.NN, AAV2.GL | [78] | |
AAV9 | [79] | |
Skeletal muscles | AAV1 | [80] |
AAV8 | [70], [80] | |
AAV9 | [80] | |
AAVrh.74 | [81] | |
Heart | AAV1 | [80] |
AAV6 | [61] | |
AAV8 | [61] | |
AAV9 | ||
AAVrh.10 | [58] | |
AAVrh.74 | [81] | |
Liver | AAV2, AAV5, AAV7, AAV8 | [82] |
AAV3B | [83] | |
AAV9 | [58] | |
AAVrh.10 | [58] | |
Pancreas | AAV2 | [66] |
AAV7 | [84] | |
Kidney | AAV3B | [83] |
AAV2, AAV5, AAV7, AAV8 | [82] | |
AAVrh74 | [81] | |
Gastro-intestinal tract | AAV6, AAV8, AAV9 | [61] |
AAV2 | [66] | |
AAV5 | [82] |