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Table 1 AAV serotypes biodistribution demonstrated in non-human primates’ studies

From: Current advances in gene therapy of mitochondrial diseases

Organ

Serotype

References

Brain

AAV2

[66],

[67],

[68]

AAV5

[69]

AAV8

[70]

AAV9

[58],

[71],

[72]

AAVrh.10

[58],

[73],

[74],

[75],

[76]

Retina

AAV5, AAV2-HBKO

[77]

AAV2.NN, AAV2.GL

[78]

AAV9

[79]

Skeletal muscles

AAV1

[80]

AAV8

[70],

[80]

AAV9

[80]

AAVrh.74

[81]

Heart

AAV1

[80]

AAV6

[61]

AAV8

[61]

AAV9

[61, 80]

AAVrh.10

[58]

AAVrh.74

[81]

Liver

AAV2, AAV5, AAV7, AAV8

[82]

AAV3B

[83]

AAV9

[58]

AAVrh.10

[58]

Pancreas

AAV2

[66]

AAV7

[84]

Kidney

AAV3B

[83]

AAV2, AAV5, AAV7, AAV8

[82]

AAVrh74

[81]

Gastro-intestinal tract

AAV6, AAV8, AAV9

[61]

AAV2

[66]

AAV5

[82]