TY - STD TI - Hacein-Bey-Abina S, Hauer J, Lim A, Picard C, Wang GP, Berry CC, Martinache C, Rieux-Laucat F, Latour S, Belohradsky BH: Efficacy of gene therapy for X-linked severe combined immunodeficiency. N Engl J Med. 363: 355-364. ID - ref1 ER - TY - JOUR AU - Gaspar, H. B. AU - Parsley, K. L. AU - Howe, S. AU - King, D. AU - Gilmour, K. C. AU - Sinclair, J. AU - Brouns, G. AU - Schmidt, M. AU - Von Kalle, C. AU - Barington, T. PY - 2004 DA - 2004// TI - Gene therapy of X-linked severe combined immunodeficiency by use of a pseudotyped gammaretroviral vector JO - Lancet VL - 364 UR - https://doi.org/10.1016/S0140-6736(04)17590-9 DO - 10.1016/S0140-6736(04)17590-9 ID - Gaspar2004 ER - TY - JOUR AU - Cavazzana-Calvo, M. AU - Hacein-Bey, S. AU - de Saint Basile, G. AU - Gross, F. AU - Yvon, E. AU - Nusbaum, P. AU - Selz, F. AU - Hue, C. AU - Certain, S. AU - Casanova, J. L. PY - 2000 DA - 2000// TI - Gene therapy of human severe combined immunodeficiency (SCID)-X1 disease JO - Science VL - 288 UR - https://doi.org/10.1126/science.288.5466.669 DO - 10.1126/science.288.5466.669 ID - Cavazzana-Calvo2000 ER - TY - JOUR AU - Miyoshi, H. AU - Smith, K. A. AU - Mosier, D. E. AU - Verma, I. M. AU - Torbett, B. E. PY - 1999 DA - 1999// TI - Transduction of human CD34+ cells that mediate long-term engraftment of NOD/SCID mice by HIV vectors JO - Science VL - 283 UR - https://doi.org/10.1126/science.283.5402.682 DO - 10.1126/science.283.5402.682 ID - Miyoshi1999 ER - TY - JOUR AU - Case, S. S. AU - Price, M. A. AU - Jordan, C. T. AU - Yu, X. J. AU - Wang, L. AU - Bauer, G. AU - Haas, D. L. AU - Xu, D. AU - Stripecke, R. AU - Naldini, L. PY - 1999 DA - 1999// TI - Stable transduction of quiescent CD34(+)CD38(-) human hematopoietic cells by HIV-1-based lentiviral vectors JO - Proc Natl Acad Sci USA VL - 96 UR - https://doi.org/10.1073/pnas.96.6.2988 DO - 10.1073/pnas.96.6.2988 ID - Case1999 ER - TY - JOUR AU - Naldini, L. AU - Blomer, U. AU - Gallay, P. AU - Ory, D. AU - Mulligan, R. AU - Gage, F. H. AU - Verma, I. M. AU - Trono, D. PY - 1996 DA - 1996// TI - In vivo gene delivery and stable transduction of nondividing cells by a lentiviral vector JO - Science VL - 272 UR - https://doi.org/10.1126/science.272.5259.263 DO - 10.1126/science.272.5259.263 ID - Naldini1996 ER - TY - JOUR AU - Burns, J. C. AU - Friedmann, T. AU - Driever, W. AU - Burrascano, M. AU - Yee, J. K. PY - 1993 DA - 1993// TI - Vesicular stomatitis virus G glycoprotein pseudotyped retroviral vectors: concentration to very high titer and efficient gene transfer into mammalian and nonmammalian cells JO - Proc Natl Acad Sci USA VL - 90 UR - https://doi.org/10.1073/pnas.90.17.8033 DO - 10.1073/pnas.90.17.8033 ID - Burns1993 ER - TY - JOUR AU - Akkina, R. K. AU - Walton, R. M. AU - Chen, M. L. AU - Li, Q. X. AU - Planelles, V. AU - Chen, I. S. PY - 1996 DA - 1996// TI - High-efficiency gene transfer into CD34+ cells with a human immunodeficiency virus type 1-based retroviral vector pseudotyped with vesicular stomatitis virus envelope glycoprotein G JO - J Virol VL - 70 ID - Akkina1996 ER - TY - JOUR AU - Mastromarino, P. AU - Conti, C. AU - Goldoni, P. AU - Hauttecoeur, B. AU - Orsi, N. PY - 1987 DA - 1987// TI - Characterization of membrane components of the erythrocyte involved in vesicular stomatitis virus attachment and fusion at acidic pH JO - J Gen Virol VL - 68 UR - https://doi.org/10.1099/0022-1317-68-9-2359 DO - 10.1099/0022-1317-68-9-2359 ID - Mastromarino1987 ER - TY - JOUR AU - Marsh, M. AU - Helenius, A. PY - 1989 DA - 1989// TI - Virus entry into animal cells JO - Adv Virus Res VL - 36 UR - https://doi.org/10.1016/S0065-3527(08)60583-7 DO - 10.1016/S0065-3527(08)60583-7 ID - Marsh1989 ER - TY - JOUR AU - Poluri, A. AU - Sutton, R. E. PY - 2008 DA - 2008// TI - Titers of HIV-based vectors encoding shRNAs are reduced by a dicer-dependent mechanism JO - Mol Ther VL - 16 UR - https://doi.org/10.1038/sj.mt.6300370 DO - 10.1038/sj.mt.6300370 ID - Poluri2008 ER - TY - JOUR AU - Ory, D. S. AU - Neugeboren, B. A. AU - Mulligan, R. C. PY - 1996 DA - 1996// TI - A stable human-derived packaging cell line for production of high titer retrovirus/vesicular stomatitis virus G pseudotypes JO - Proc Natl Acad Sci USA VL - 93 UR - https://doi.org/10.1073/pnas.93.21.11400 DO - 10.1073/pnas.93.21.11400 ID - Ory1996 ER - TY - JOUR AU - Rebel, V. I. AU - Tanaka, M. AU - Lee, J. S. AU - Hartnett, S. AU - Pulsipher, M. AU - Nathan, D. G. AU - Mulligan, R. C. AU - Sieff, C. A. PY - 1999 DA - 1999// TI - One-day ex vivo culture allows effective gene transfer into human nonobese diabetic/severe combined immune-deficient repopulating cells using high-titer vesicular stomatitis virus G protein pseudotyped retrovirus JO - Blood VL - 93 ID - Rebel1999 ER - TY - JOUR AU - Kamel-Reid, S. AU - Zhang, T. AU - Wells, R. A. PY - 2003 DA - 2003// TI - Expression of NPM-RARalpha fusion gene in hematopoietic cells confers sensitivity to troglitazone-induced apoptosis JO - Oncogene VL - 22 UR - https://doi.org/10.1038/sj.onc.1206696 DO - 10.1038/sj.onc.1206696 ID - Kamel-Reid2003 ER - TY - STD TI - Ichim CV, Atkins HL, Iscove NN, Wells RA: Identification of a role for the nuclear receptor EAR-2 in the maintenance of clonogenic status within the leukemia cell hierarchy. Leukemia. ID - ref15 ER - TY - JOUR AU - Yamada, K. AU - McCarty, D. M. AU - Madden, V. J. AU - Walsh, C. E. PY - 2003 DA - 2003// TI - Lentivirus vector purification using anion exchange HPLC leads to improved gene transfer JO - Biotechniques VL - 34 ID - Yamada2003 ER - TY - JOUR AU - Reiser, J. PY - 2000 DA - 2000// TI - Production and concentration of pseudotyped HIV-1-based gene transfer vectors JO - Gene Ther VL - 7 UR - https://doi.org/10.1038/sj.gt.3301188 DO - 10.1038/sj.gt.3301188 ID - Reiser2000 ER -